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clinical trial

2 papers tagged “clinical trial

MedicineNew England Journal of Medicine · Dec 2020 Open access

Safety and Efficacy of the BNT162b2 mRNA Covid-19 Vaccine

Fernando P. Polack, Stephen J. Thomas, Nicholas Kitchin, Judith Absalon, Alejandra Gurtman, Stephen Lockhart, et al.

This multinational, randomized, placebo-controlled phase 2/3 trial evaluated the safety and efficacy of two 30-µg doses of the BNT162b2 lipid-nanoparticle mRNA vaccine, given 21 days apart, in 43,548 participants 16 years of age or older. Among those without prior SARS-CoV-2 infection, the vaccine conferred 95% protection against laboratory-confirmed Covid-19 beginning at least 7 days after the second dose. The safety profile over a median of about two months was characterized by short-lived, mostly mild-to-moderate reactions, with a low incidence of serious adverse events comparable to placebo.

BiologyNew England Journal of Medicine · Feb 2018 Open access

Tisagenlecleucel in Children and Young Adults with B-Cell Lymphoblastic Leukemia

Shannon L. Maude, Theodore W. Laetsch and Jochen Buechner

This paper reports the pivotal global phase 2 ELIANA trial of tisagenlecleucel, an anti-CD19 chimeric antigen receptor (CAR) T-cell therapy, in children and young adults with relapsed or refractory B-cell acute lymphoblastic leukemia. It demonstrated high rates of durable remission and supported the first FDA approval of a CAR-T cell therapy. The study also characterized the safety profile, including cytokine release syndrome.